VS: Google Alert - rare disease

[Nils K Oeijord]

News 3 new results for rare disease

Alexion snags latest 'breakthrough' coup with PhIII rare-disease drug FierceBiotech The FDA has added another regulatory coup for Alexion's ($ALXN) late-stage program for asfotase alfa, an enzyme replacement therapy for extremely rare cases of a metabolic disease known as hypophosphatasia. Already handed an orphan drug ... See all stories on this topic »

Woman advocates for those with rare disease Alton Telegraph Kraig Klenke, pictured with his family, was only 3 years old when he was diagnosed with a rare genetic disorder known as MPS, short for mucoploysaccharidosis. The disease causes progressive damage to cells in the body, and results in the severe ... See all stories on this topic »

UNMC treats toddlers' rare disease KETV Omaha ... ASmall Text; AMedium Text; ALarge Text. Child inherits rare intestinal disease. A 2-year-old from Texas is seeking medical care at the University of Nebraska Medical Center for a rare intestinal disorder she inherited from her mother during the ... See all stories on this topic »

---

Tip: Use site restrict in your query to search within a site (site:nytimes.com or site:.edu). Learn more.

Delete this alert.
Create another alert.
Manage your alerts.